OALib Journal期刊
ISSN: 2333-9721
费用:99美元
A multicenter comparison of quantification methods for antisense oligonucleotide-induced DMD exon 51 skipping in Duchenne muscular dystrophy cell cultures
DOI: 10.1371/journal.pone.0204485
Alessandra Ferlini ,
Annemieke Aartsma-Rus ,
Estibaliz Ruiz-Del-Yerro ,
Francesco Muntoni ,
George Dickson ,
Hana Osman ,
Iker Garcia-Jimenez ,
Jelle J. Goeman ,
Kamel Mamchaoui ,
Karen Anthony ,
Linda Popplewell ,
Maria Sofia Falzarano ,
Monika Hiller ,
Nicole A. Datson ,
Pietro Spitali ,
Ruurd C. Verheul ,
Valentina Sardone ,
Virginia Arechavala-Gomeza
Abstract:
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