CAVAZZANA-CALVO M, HACEIN-BEY S, DE SAINT BASILE G. Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease [J]. Science, 2000.669-672.
[2]
HACEIN-BEY-ABINA S, LE DEIST F, CARLIER F. Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy [J]. New England Journal of Medicine, 2002.1185-1193.doi:10.1056/NEJMoa012616.
[3]
KAY M A, MANNO C S, RAGNI M V. Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector [J]. Nature Genetics, 2000.257-261.
[4]
AIUTI A, SLAVIN S, AKER M. Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning [J]. Science, 2002.2410-2413.
[5]
FISHER K J. A novel adenovirus-adeno-associated virus hybrid vector that displays efficient rescue and delivery of the AAV genome [J]. Human Gene Therapy, 1996(7):2079-2087.
LEHRMAN S. Virus treatment questioned after gene therapy death [J]. Nature, 1999.517-518.
[8]
GONCALVES M A, VELDE I, JANSSEN J M. Efficient generation and amplification of high-capacity adeno-associated virus/adenovirus hybrid vectors [J]. Virology, 2002.10734-10744.
[9]
GONCALVES MAFV, NIEROP G P, TIJSSEN M R. Transfer of the full-length dystrophin-coding sequence into muscle cells by a dual high-capacity hybrid viral vector with site-specific integration ability [J]. Virology, 2005(5):3146-3162.
[10]
SHAYAKHMETOV D M, CARISON C A, STECHER H. A high-capacity, capsid-modified hybrid adenovirus/adeno-associated virus vector for stable transduction of human hematopoietic cells [J]. Virology, 2002.1135-1143.doi:10.1128/JVI.76.3.1135-1143.2002.
CHECK E. Gene therapy put on hold as third child develops cancer [J]. NATURE, 2005.561.
[14]
FRAEFEl C, BREAKEFIELD X O. Hybrid vectors:A new generation of virus-based vectors designed to control the cellular fate of delivered genes [J]. Gen Therapy, 1997(4):1281-1283.
[15]
RECCHIA A, PARKS R J, LAMARTINA S. Site-specific integration mediated by a hybrid adenovirus/adenoassociated virus vector [J]. Proceedings of the National Academy of Sciences(USA), 1999.2615-2620.
[16]
LIEBER A, STEINWAERDER D S, CARLSON C A. Integrating adenovirus-adeno-associated virus hybrid vectors devoid of all viral genes [J]. Virology, 1999.9314-9324.
