%0 Journal Article
%T Therapeutic Prospects for Friedreich¡¯s Ataxia
%J -
%D 2019
%R https://doi.org/10.1016/j.tips.2019.02.001
%X Friedreich¡¯s ataxia (FRDA) is a progressive disease affecting multiple organs that is caused by systemic insufficiency of the mitochondrial protein frataxin. Current therapeutic strategies aim to elevate frataxin levels and/or alleviate the consequences of frataxin deficiency. Recent significant advances in the FRDA therapeutic pipeline are bringing patients closer to a cure
%U https://www.cell.com/trends/pharmacological-sciences/fulltext/S0165-6147(19)30032-X