%0 Journal Article %T In utero and postnatal VX-770 administration rescues multiorgan disease in a ferret model of cystic fibrosis %J - %D 2018 %R 10.1126/scitranslmed.aau7531 %X In utero and early postnatal functional rescue of cystic fibrosis transmembrane conductance regulator improves survival in cystic fibrosis ferrets %U http://stm.sciencemag.org/content/11/485/eaau7531