%0 Journal Article
%T Novel treatments for rare rheumatologic disorders: analysis of the impact of 30£¿years of the US orphan drug act
%A Anette Lampert
%A Georg F. Hoffmann
%A Markus Ries
%A Thomas Lutz
%J Archive of "Orphanet Journal of Rare Diseases".
%D 2016
%R 10.1186/s13023-016-0443-x
%X Rare rheumatologic diseases are a heterogeneous group of conditions associated with high morbidity. As a whole group, rare rheumatologic diseases afflict millions of people demanding for effective therapies. Therefore, we analyzed the impact of the US Orphan Drug Act on the development of anti-rheumatic orphan drugs
%K Orphan drug act
%K Orphan drug development
%K Rare disease
%K Rare rheumatologic disease
%U https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4866287/