%0 Journal Article %T Duchenne型肌营养不良基因治疗研究进展<br>A review of gene therapy for Duchenne muscular dystrophy %A 董奇超 %A 陈慧敏 %A 金欣< %A br> %A DONG Qi-Chao %A CHEN Hui-Min %A JIN Xin %J 中国当代儿科杂志 %D 2018 %R 10.7499/j.issn.1008-8830.2018.08.017 %K Duchenne型肌营养不良 %K 腺相关病毒 %K 肌营养不良蛋白相关蛋白 %K 成簇规律间隔的短回文重复序列技术 %K 儿童 %K < %K br> %K Duchenne muscular dystrophy %K Adeno-associated virus %K Utrophin %K Clustered regularly interspaced short palindromic repeat %K Child %U http://www.zgddek.com/CN/abstract/abstract14584.shtml